DOCUMENT AND ENTITY INFORMATION Document Type Document Quarterly Report Document Period End Date Document Transition Report Entity File Number Entity Registrant Name Entity Incorporation, State or Country Code Entity Tax Identification Number Entity Address, Address Line One Entity Address State Or Province Entity Address, City or Town Entity Address, Postal Zip Code City Area Code Local Phone Number Title of 12(b) Security Trading Symbol Security Exchange Name Entity Current Reporting Status Entity Interactive Data Current Entity Filer Category Entity Small Business Entity Emerging Growth Company Entity Shell Company Entity Common Stock, Shares Outstanding Entity Central Index Key Current Fiscal Year End Date Document Fiscal Year Focus Document Fiscal Period Focus Amendment Flag Condensed Balance Sheets Statement [Table] Statement [Line Items] Statement Assets [Abstract] Assets Assets, Current [Abstract] Current assets Cash and Cash Equivalents, at Carrying Value Cash and cash equivalents Cash and cash equivalents Marketable Securities Marketable securities, available for sale Prepaid Expense and Other Assets, Current Prepaid expenses and other assets Assets, Current Total current assets Property, Plant and Equipment, Net Property and equipment, net Property and equipment, net Operating Lease, Right-of-Use Asset Operating lease right-of-use asset Assets Total assets Liabilities and Equity [Abstract] Liabilities and stockholders' equity Liabilities, Current [Abstract] Current liabilities Accounts Payable, Current Accounts payable Employee-related Liabilities, Current Accrued compensation Accrued Liabilities, Current Accrued other expenses Total accrued other expenses Accrued Income Taxes, Current Accrued taxes Operating Lease, Liability, Current Operating lease liability, current portion Disposal Group, Including Discontinued Operation, Liabilities, Current Current liabilities held for sale Liabilities derecognized Liabilities, Current Total current liabilities Operating Lease, Liability, Noncurrent Operating lease liability, net of current portion Other Liabilities, Noncurrent Other long term liabilities Liabilities Total liabilities Commitments and Contingencies Commitments and contingencies (see note 5) Stockholders' Equity, Including Portion Attributable to Noncontrolling Interest [Abstract] Stockholders' equity: Preferred Stock, Value, Issued Preferred stock, $.0001 par value per share; 200,000,000 shares authorized and no shares issued or outstanding as of September 30, 2026 and December 31, 2025 Common Stock, Value, Issued Common stock, $.0001 par value per share; 1,000,000,000 shares authorized as of September 30, 2026 and December 31, 2025; 109,457,922 shares and 106,249,579 shares issued and outstanding as of September 30, 2026 and December 31, 2025, respectively Additional Paid in Capital Additional paid-in capital Accumulated Other Comprehensive Income (Loss), Net of Tax Accumulated other comprehensive (loss) income Retained Earnings (Accumulated Deficit). Retained earnings (accumulated deficit) Stockholders' Equity Attributable to Parent Balance, Ending Balance, Beginning Total stockholders' equity Liabilities and Equity Total liabilities and stockholders' equity Preferred Stock, Par or Stated Value Per Share Par value of preferred stock (in dollars per share) Preferred stock, par value Preferred Stock, Shares Authorized Preferred stock, shares authorized (in shares) Preferred Stock, Shares Issued Preferred stock, shares issued Preferred Stock, Shares Outstanding Preferred stock, shares outstanding Common Stock, Par or Stated Value Per Share Common stock, par value Par value of common stock (in dollars per share) Common Stock, Shares Authorized Common stock, shares authorized Common stock authorized (in shares) Common Stock, Shares, Issued Common stock, shares issued Common Stock, Shares, Outstanding Balance, Ending (in shares) Balance, Beginning (in shares) Common stock, shares outstanding Condensed Statements of Operations and Comprehensive Income (Loss) Operating Expenses [Abstract] Operating expenses Operating expenses: Research and Development Expense Research and development General and Administrative Expense General and administrative Operating Expenses Total operating expenses Operating Income (Loss) Loss from operations Other Nonoperating Income (Expense) [Abstract] Other income Interest Income, Other Interest income Other Nonoperating Income Other income Other income Disposal Group, Not Discontinued Operation, Gain (Loss) on Disposal Gain on the Sevasemten Sale Gain on the Sevasemten Sale Gain on the Sevasemten Sale Nonoperating Income (Expense) Total other income Income (Loss) from Continuing Operations before Income Taxes, Noncontrolling Interest Income (loss) before income tax expense Income Tax Expense (Benefit) Income tax expense Net income (loss) Net income (loss) Other Comprehensive Income (Loss), Net of Tax, Portion Attributable to Parent [Abstract] Other comprehensive income (loss): OCI, Debt Securities, Available-for-Sale, Gain (Loss), after Adjustment and Tax Unrealized (loss) gain on available-for-sale securities, net Comprehensive Income (Loss), Net of Tax, Attributable to Parent Total comprehensive income (loss) Earnings Per Share, Basic Basic earnings (loss) per share Basic earnings (loss) per share (in dollars per share) Earnings Per Share, Diluted Diluted earnings (loss) per share Diluted earnings (loss) per share (in dollars per share) Weighted Average Number of Shares Outstanding, Basic Weighted-average shares outstanding used in basic earnings (loss) per share Weighted-average shares outstanding used in basic earnings (loss) per share (in shares) Weighted Average Number of Shares Outstanding, Diluted Weighted-average shares outstanding used in diluted earnings (loss) per share Weighted-average shares outstanding used in diluted earnings (loss) per share (in shares) Condensed Statements of Stockholders' Equity Equity Components [Axis] Equity Component [Domain] Common Stock Additional Paid-in Capital Accumulated Other Comprehensive Income (Loss) Retained Earnings (Accumulated Deficit) Increase (Decrease) in Stockholders' Equity [Roll Forward] Stock Issued During Period, Value, New Issues Issuance of common stock, net of offering costs Stock Issued During Period, Shares, New Issues Issuance of common stock, net of offering costs (in shares) Shares issued Stock Issued During Period, Value, Stock Options Exercised Exercise of stock options Share-based Compensation Arrangement by Share-based Payment Award, Options, Exercises in Period Exercise of stock options (shares) Shares Issued, Value, Share-Based Payment Arrangement, after Forfeiture Exercise of stock options and vesting of restricted stock units Shares Issued, Shares, Share-Based Payment Arrangement, after Forfeiture Exercise of stock options and vesting of restricted stock units (in shares) Stock Issued During Period, Value, Employee Stock Purchase Plan Purchase of common stock under Employee Stock Purchase Plan Stock Issued During Period, Shares, Employee Stock Purchase Plans Purchase of common stock under Employee Stock Purchase Plan (in shares) APIC, Share-based Payment Arrangement, Option, Increase for Cost Recognition Stock-based compensation Other Comprehensive Income (Loss), Net of Tax Other comprehensive income (loss) Condensed Statements of Cash Flows Net Cash Provided by (Used in) Operating Activities [Abstract] Cash flows from operating activities Net Income (Loss), Including Portion Attributable to Noncontrolling Interest Net income (loss) Adjustments to Reconcile Net Income (Loss) to Cash Provided by (Used in) Operating Activities [Abstract] Adjustments to reconcile net income (loss) to net cash used in operating activities: Depreciation Depreciation expense Depreciation Share-based Payment Arrangement, Noncash Expense Stock-based compensation Accretion (Amortization) of Discounts and Premiums, Investments Accretion of discount on marketable securities, net Finance Lease, Right-of-Use Asset, Amortization Amortization of right-of-use asset Increase (Decrease) in Operating Capital [Abstract] Changes in assets and liabilities: Increase (Decrease) in Prepaid Expense and Other Assets Prepaid expenses and other assets Increase (Decrease) in Accounts Payable Accounts payable Increase (Decrease) in Employee Related Liabilities Accrued compensation Increase (Decrease) in Other Accrued Liabilities Accrued other expenses and other liabilities Increase (Decrease) in Accrued Taxes Payable Accrued taxes Increase (Decrease) in Operating Lease Liability Lease liability Net Cash Provided by (Used in) Operating Activities Net cash used in operating activities Net Cash Provided by (Used in) Investing Activities [Abstract] Cash flows from investing activities Payments to Acquire Marketable Securities Purchases of marketable securities Proceeds from Sale of Held-to-Maturity Securities Sales of marketable securities Proceeds from Maturities, Prepayments and Calls of Held-to-Maturity Securities Maturities of marketable securities Proceeds from Sale of Productive Assets Proceeds from the Sevasemten Sale, net of transaction costs Payments to Acquire Property, Plant, and Equipment Purchases of property and equipment Net Cash Provided by (Used in) Investing Activities Net cash provided by (used in) investing activities Net Cash Provided by (Used in) Financing Activities [Abstract] Cash flows from financing activities Proceeds from Issuance of Common Stock Proceeds from issuance of common stock, net of offering costs Proceeds from issuance of common stock Proceeds from Stock Options Exercised Exercise of stock options Proceeds from Stock Plans Proceeds from Employee Stock Purchase Plan Net Cash Provided by (Used in) Financing Activities Net cash provided by financing activities Cash and Cash Equivalents, Period Increase (Decrease) Net change in cash and cash equivalents Cash, Cash Equivalents, Restricted Cash and Restricted Cash Equivalents Cash and cash equivalents at end of period Cash and cash equivalents at beginning of period Other Noncash Investing and Financing Items [Abstract] Supplemental disclosures of non-cash investing activities: Capital Expenditures Incurred but Not yet Paid Property and equipment purchases included in accounts payable Supplemental Cash Flow Information [Abstract] Supplemental disclosures of cash flow information: Income Tax Paid, after Refund Received Cash paid for income taxes, net Amount of cash outflow during the period for transferable federal income tax credits. Payments For Transferable Federal Income Tax Credits Payments to purchase transferable federal income tax credits DESCRIPTION OF BUSINESS Nature of Operations [Text Block] DESCRIPTION OF BUSINESS SUMMARY OF SIGNIFICANT ACCOUNTING POLICIES Significant Accounting Policies [Text Block] SUMMARY OF SIGNIFICANT ACCOUNTING POLICIES PREFERRED STOCK AND COMMON STOCK Convertible preferred stock The entire disclosure for temporary equity. Temporary Equity [Text Block] PREFERRED STOCK AND COMMON STOCK STOCK-BASED COMPENSATION AWARDS Share-based Payment Arrangement [Text Block] STOCK-BASED COMPENSATION AWARDS COMMITMENTS AND CONTINGENCIES. Commitments and Contingencies Disclosure [Text Block] COMMITMENTS AND CONTINGENCIES NET EARNINGS (LOSS) PER SHARE Earnings Per Share [Text Block] NET EARNINGS (LOSS) PER SHARE PROPERTY AND EQUIPMENT Property, Plant and Equipment Disclosure [Text Block] PROPERTY AND EQUIPMENT ACCRUED OTHER EXPENSES Accounts Payable, Accrued Liabilities, and Other Liabilities Disclosure, Current [Text Block] ACCRUED OTHER EXPENSES SEGMENT REPORTING Segment Reporting Disclosure [Text Block] SEGMENT REPORTING ASSET DISPOSITIONS Disposal Groups, Including Discontinued Operations, Disclosure [Text Block] ASSET DISPOSITIONS INCOME TAXES Income Tax Disclosure [Text Block] INCOME TAXES Basis of Accounting, Policy [Policy Text Block] Basis of Presentation Marketable Securities, Policy [Policy Text Block] Marketable Securities, Available for Sale Disclosure of accounting policy on contingent consideration. Contingent Consideration, Policy [Policy Text Block] Contingent Consideration New Accounting Pronouncements, Policy [Policy Text Block] Recently Adopted Accounting Standards Disclosure of accounting policy for recently issued Accounting Standards not yet adopted. New Accounting Pronouncements, Not Yet Adopted Policy [Policy Text Block] Accounting Standards Not Yet Adopted Marketable Securities [Table Text Block] Schedule of financial assets measured at fair value on a recurring basis by level within the fair value hierarchy Share-based Payment Arrangement, Expensed and Capitalized, Amount [Table Text Block] Schedule of stock-based compensation expense Schedule of Earnings Per Share, Basic and Diluted [Table Text Block] Schedule of computation of basic and diluted net earnings (loss) per share Schedule of Antidilutive Securities Excluded from Computation of Earnings Per Share [Table Text Block] Schedule of potentially dilutive securities Property, Plant and Equipment [Table Text Block] Schedule of property plant and equipment Schedule of Accrued Liabilities [Table Text Block] Schedule of accrued other expenses Schedule of Segment Reporting Information, by Segment [Table Text Block] Schedule of revenue and expenses for the operating segment to consolidated amounts Subsidiary or Equity Method Investee, Sale of Stock by Subsidiary or Equity Investee [Table] Sale of Stock [Axis] Sale of Stock [Domain] A type of follow-on offering of stock utilized by publicly traded companies in order to raise capital over time. At-the-market program Statistical Measurement [Axis] Statistical Measurement [Domain] Maximum Maximum Disposal Group Classification [Axis] Disposal Group Classification [Domain] Disposal Group, Disposed of by Sale, Not Discontinued Operations [Member] Disposed of by sale Scenario [Axis] Scenario [Domain] Represents approval for Becker muscular dystrophy for adult and adolescent populations. Approval For Becker Muscular Dystrophy, Adult And Adolescent Populations [Member] Approval For Becker Muscular Dystrophy, Adult And Adolescent Populations Represents approval for Becker muscular dystrophy for adult populations. Approval For Becker Muscular Dystrophy, Adult Populations [Member] Approval For Becker Muscular Dystrophy, Adult Populations Represents approval for Duchenne muscular dystrophy. Approval For Duchenne Muscular Dystrophy [Member] Approval For Duchenne Muscular Dystrophy Subsidiary, Sale of Stock [Line Items] DESCRIPTION OF BUSINESS It represents the cash, cash equivalents and marketable securities Cash, Cash Equivalents And Marketable Securities Cash, cash equivalents and marketable securities Share Price Share price Gross proceeds from the issuance of common stock. Gross Proceeds from Issuance of Common Stock Gross proceeds