v3.26.1
Condensed Consolidated Balance Sheets (Unaudited) - USD ($)
$ in Thousands
6 Months Ended
Jun. 30, 2026
Dec. 31, 2025
Current assets:    
Cash and cash equivalents $ 19,171 $ 18,008
Investments in marketable short-term securities 73,454 73,463
Accounts receivable 369 1,447
Receivable from Genevant license 179,373 0
Prepaid expenses and other current assets 1,516 1,538
Total current assets 273,883 94,456
Property and equipment, net of accumulated depreciation and impairment of $235 (December 31, 2025: $213) 10 32
Other non-current assets 132 130
Total assets 274,025 94,618
Current liabilities:    
Accounts payable and accrued liabilities 2,850 5,459
Lease liability, current 514 547
Total current liabilities 3,364 6,006
Liability related to sale of future royalties 3,111 3,442
Contingent consideration 8,817 8,395
Lease liability, non-current 0 199
Total liabilities 15,292 18,042
Stockholders’ equity    
Issued and outstanding: 197,634,118 (December 31, 2025: 192,531,225) 1,448,177 1,421,429
Additional paid-in capital 74,321 83,318
Deficit (1,215,521) (1,380,073)
Accumulated other comprehensive loss (48,244) (48,098)
Total stockholders’ equity 258,733 76,576
Total liabilities and stockholders’ equity $ 274,025 $ 94,618
Common Stock, Shares Authorized, Unlimited [Fixed List] Unlimited