v3.26.1
Segment Information (Tables)
6 Months Ended
Jun. 30, 2026
Segment Reporting [Abstract]  
Summary of Segment Information

The following table reconciles segment direct profit or loss to the Company’s condensed consolidated results (in thousands):

 

 

Three Months Ended June 30,

 

 

Six Months Ended June 30,

 

 

 

2026

 

 

2025

 

 

2026

 

 

2025

 

Revenue

 

$

9,325

 

 

$

13,817

 

 

$

15,554

 

 

$

172,386

 

Zorevunersen(1)

 

 

28,243

 

 

 

11,382

 

 

 

48,097

 

 

 

29,056

 

ADOA(1)

 

 

2,697

 

 

 

1,747

 

 

 

4,555

 

 

 

2,140

 

SYNGAP1(1)

 

 

1,073

 

 

 

818

 

 

 

1,818

 

 

 

1,160

 

MECP2(1)

 

 

 

 

 

(200

)

 

 

 

 

 

(53

)

Other external program costs

 

 

3,990

 

 

 

1,841

 

 

 

7,169

 

 

 

3,670

 

Payroll and other personnel costs - R&D (2)

 

 

18,218

 

 

 

11,618

 

 

 

34,336

 

 

 

22,629

 

Payroll and other personnel costs - SG&A (2)

 

 

13,318

 

 

 

8,979

 

 

 

24,375

 

 

 

17,908

 

Other non-program costs - R&D (3)

 

 

1,628

 

 

 

1,615

 

 

 

3,308

 

 

 

3,022

 

Other non-program costs - SG&A (3)

 

 

5,587

 

 

 

3,317

 

 

 

10,742

 

 

 

8,914

 

Interest expense

 

 

(17

)

 

 

(3

)

 

 

(41

)

 

 

(3

)

Interest income

 

 

3,520

 

 

 

3,792

 

 

 

6,939

 

 

 

6,681

 

Other income

 

 

308

 

 

 

28

 

 

 

327

 

 

 

57

 

Provision for income taxes

 

 

 

 

 

 

 

 

 

 

 

(1,278

)

Segment net income (loss)

 

$

(61,618

)

 

$

(23,483

)

 

$

(111,621

)

 

$

89,397

 

(1) Includes external research and development and sales, general and administrative expenses associated with programs.

(2) Includes salaries, benefits and other personnel related expenses, including stock based compensation expense, of relevant personnel.

(3) Includes costs incurred for conducting non-program activities related to Company activities.